Patient Reported Outcome Measures (PROMs)

This research was conducted by a team of researchers and published in the Journal of Patient-Reported Outcomes. The study explored the use of PROMs in routine clinical care and the potential benefits and challenges associated with their implementation. The research showed that while PROMs have the potential to improve patient care, there are significant challenges that need to be addressed to ensure their effective use in routine clinical practice.

This research was conducted by a team of researchers and published in the Orphanet Journal of Rare Diseases. The study focused on the development and validation of a specific PROM for Gaucher disease type 1 (GD1), a rare disease. The research showed that the developed PROM is a significant step forward in measuring the impact of GD and its treatment, and further validation in different populations is needed to confirm its appropriateness.